Euractiv.com Est. 1min 27-10-2023 (updated: 04-12-2023 ) Content-Type: Sponsored By Sponsored By An organization or individual has paid to be connected to this work but did not approve or review it. Gene therapies can address the cause of a disease from its genetic root. [SHUTTERSTOCK/vchal] Euractiv is part of the Trust Project >>> Languages: Français | Deutsch | Ελληνικά | Spanish | ItalianPrint Email Facebook X LinkedIn WhatsApp Telegram Gene therapies can transform the approach to rare diseases and improve the quality of life for patients. But developing and accessing them is hampered by regulatory burdens, cost and reimbursment schemes. In this special report, Euractiv takes a look at gene treatment approaches across countries, and examines the EU’s approach to such therapies for rare diseases. Download PDF EU needs to step up to unleash gene therapies potential, stakeholders say News | Health 27-10-2023 Est. 5minWhile gene therapies have the potential to transform the approach to rare diseases and improve the quality of life for patients, stakeholders and patients complain that they are very expensive to develop and difficult to access. In France, gene therapy suffers from weak economic model News | Health 03-11-2023 Est. 5minFrance is one of the most advanced countries for gene therapies, both in Europe and worldwide. However, the lack of funding and the economic fragility of the sector are holding back the development of these innovative treatments. Italy’s advanced therapy journey News | Health 08-11-2023 Est. 7minAdvanced Medicinal Therapies (ATMPs), including gene and cell therapies, offer treatment options for patients suffering from rare or ultra-rare diseases. Italy is learning to see expenditure on advanced therapy drugs as an investment but the EU’s pharmaceutical revision is causing concerns among Italian stakeholders. Greek legal framework fails to address complexities of access to gene therapies News | Health 10-11-2023 Est. 6minThe Greek legislative framework lacks concrete solutions to advance gene therapies and improve access for patients, with several challenges - including financial support, treatment availability and stakeholder cooperation - remaining. Rare disease patients across Spain don’t have the same access to treatments News | Health 29-11-2023 Est. 5minAccess to quick and accurate diagnosis and affordable drugs in Spain varies across the regions and depending on patients’ economic status. German researchers welcome national, EU support for gene therapy research News | Health 30-11-2023 Est. 5minNational and EU-level support goes a long way towards supporting research into gene therapies against rare diseases, according to German researchers, who said however that Europe still lags behind North American countries on innovation in this area.
