The complexity and rewards of gene treatments for rare diseases


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Gene therapies can address the cause of a disease from its genetic root. [SHUTTERSTOCK/vchal]

Gene therapies can transform the approach to rare diseases and improve the quality of life for patients. But developing and accessing them is hampered by regulatory burdens, cost and reimbursment schemes.

In this special report, Euractiv takes a look at gene treatment approaches across countries, and examines the EU’s approach to such therapies for rare diseases.

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